Abstract
We describe a patient with Fanconi-Bickel syndrome diagnosed by clinical manifestations and the identification of a novel mutation in the GLUT 2 gene. She was initially diagnosed with neonatal diabetes mellitus due to hyperglycaemia and glycosuria at 3 days of life. In addition, newborn screening for galactosaemia revealed hypergalactosaemia. Thereafter, she was managed with lactose-free milk and insulin therapy. However, she failed to grow and her liver became progressively enlarged. Her liver function deteriorated with increased prothrombin time. A liver biopsy done at age 9 months showed micronodular cirrhosis with marked fatty changes and she succumbed to hepatic failure with pneumonia at 10 months of age. DNA sequencing analysis of the GLUT 2 gene using her genomic DNA revealed a novel mutation in codon 5, lysine5 stop(K5X).
MeSH Terms
Diabetes Mellitus/blood,genetics,therapy
Fanconi Syndrome/genetics,physiopathology
Galactose/blood
Gene Expression Regulation
Glucose Transporter Type 2
Glycogen Storage Disease/genetics,pathology
Humans
Infant
Liver/physiopathology
Monosaccharide Transport Proteins/genetics
Mutation
Chemicals
Glucose Transporter Type 2
Monosaccharide Transport Proteins
Galactose
Authors & Affiliations
4 authors, click to expand affiliations / ORCID
Yoo Han-Wook
Department of Paediatrics, Asan Medical College of Medicine, Seoul, Korea.
[email protected]
Shin Young-Lim
Seo Eul-Ju
Kim Gu-Hwan
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