Abstract
While microRNAs (miRNAs) are recognized as playing a critical role in regulating eukaryotic gene expression, both the mechanism by which these small, noncoding RNAs function and the genes they target remain elusive. Previous studies have shown that short, single-stranded 2'-O-methyl-modified oligonucleotides that are complementary to mature microRNA sequences can interact with the miRNA-RISC nucleoprotein complex and weakly inhibit miRNA function. Here we report the identification of secondary structural elements that enhance the potency of these molecules. Incorporation of highly structured, double-stranded flanking regions around the reverse complement core significantly increases inhibitor function and allows for multi-miRNA inhibition at subnanomolar concentrations. The improved functionality of these double-stranded miRNA inhibitors may provide insights into the miRNA mechanism by suggesting the possible importance of such structures in or near endogenous miRNA target sites.
MeSH Terms
Cell Line
Drug Design
Enzyme Inhibitors/chemistry,pharmacology
Genetic Techniques
Humans
MicroRNAs/antagonists & inhibitors
RNA, Antisense/chemistry,genetics
RNA, Double-Stranded/chemistry
RNA-Induced Silencing Complex/antagonists & inhibitors
Structure-Activity Relationship
Chemicals
Enzyme Inhibitors
MicroRNAs
RNA, Antisense
RNA, Double-Stranded
RNA-Induced Silencing Complex
Authors & Affiliations
8 authors, click to expand affiliations / ORCID
Vermeulen Annaleen
Thermo Fisher Scientific, Dharmacon Products, Lafayette, Colorado 80026, USA.
[email protected]
Robertson Barbara
Dalby Andrew B
Marshall William S
Karpilow Jon
Leake Devin
Khvorova Anastasia
Baskerville Scott
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