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PMID: 30652356 Published · ppublish English Journal Article Research Support, Non-U.S. Gov't

Using simulation studies to evaluate statistical methods.

Statistics in medicine ·Vol. 38 ·No. 11 ·2019-00-20 ·Pages 2074-2102

Morris TP, White IR, Crowther MJ

Abstract

Simulation studies are computer experiments that involve creating data by pseudo-random sampling. A key strength of simulation studies is the ability to understand the behavior of statistical methods because some "truth" (usually some parameter/s of interest) is known from the process of generating the data. This allows us to consider properties of methods, such as bias. While widely used, simulation studies are often poorly designed, analyzed, and reported. This tutorial outlines the rationale for using simulation studies and offers guidance for design, execution, analysis, reporting, and presentation. In particular, this tutorial provides a structured approach for planning and reporting simulation studies, which involves defining aims, data-generating mechanisms, estimands, methods, and performance measures ("ADEMP"); coherent terminology for simulation studies; guidance on coding simulation studies; a critical discussion of key performance measures and their estimation; guidance on structuring tabular and graphical presentation of results; and new graphical presentations. With a view to describing recent practice, we review 100 articles taken from Volume 34 of Statistics in Medicine, which included at least one simulation study and identify areas for improvement.

Keywords
Monte Carlo graphics for simulation simulation design simulation reporting simulation studies
MeSH Terms
Bias Biostatistics/methods Computer Simulation Guidelines as Topic Models, Statistical Monte Carlo Method Research Design
Authors & Affiliations
3 authors, click to expand affiliations / ORCID
Morris Tim P ORCID
London Hub for Trials Methodology Research, MRC Clinical Trials Unit at UCL, London, United Kingdom.
White Ian R ORCID
London Hub for Trials Methodology Research, MRC Clinical Trials Unit at UCL, London, United Kingdom.
Crowther Michael J ORCID
Biostatistics Research Group, Department of Health Sciences, University of Leicester, Leicester, United Kingdom.
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Article Info
Journal
Statistics in medicine
Abbr.
Stat Med
ISSN
1097-0258
Published
2019-00-20
Epub
2019-00-16
Pages
2074-2102
Language
English
Region
England
NLM ID
8215016
PMCID
PMC6492164
Subset
IM
Grants
Medical Research Council · MC_UU_12023/21 · United Kingdom
Medical Research Council · MC_UU_12023/29 · United Kingdom
Medical Research Council · MR/P015433/1 · United Kingdom
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